genetic disorder - Search News

Pfizer, gene therapy

FDA approves Pfizer’s first gene therapy for rare inherited bleeding disorder

The Food and Drug Administration on Friday approved Pfizer’s treatment for a rare genetic bleeding disorder, making it the company’s first-ever gene therapy to win clearance in the U.S.

Teen Cured of Rare Genetic Disorder: World's First Case

Discover how a groundbreaking medical team cured Kai, 13, of WILD syndrome, marking a milestone in rare disorder treatment.

Indiatimes on MSN · 12d

8 of family with rare genetic disorder in Rajasthan vote from home

Bhanwar Lal's family with disabled members voted from home in Sarothiya village under Sujangarh assembly. They rely on farming and disability pensions

Bloomberg L.P. · 3h

Pfizer’s First Gene Therapy Gets Approval for Clotting Disorder

Pfizer Inc. won US approval for its first gene therapy, expanding into a promising field of medicine that has proved to be a challenging business.

US approves gene therapy treatment for hemophilia

Pharmaceutical giant Pfizer has received US approval for a gene therapy against a form of hemophilia, a rare and inherited blood clotting disorder, the company said Friday.Pfizer's genetic therapy targets hemophilia B,

MarketWatch · 3h

Pfizer Gets FDA OK For Beqvez Gene Therapy for Hemophilia B

By Colin Kellaher Pfizer has won Food and Drug Administration approval of Beqvez, a one-time gene therapy for certain patients with the inherited

4h

Our daughter, 11, died of rare disorder – now we’re raising funds at Glasgow Kiltwalk after sister got same diagnosis

A COUPLE whose “bravest most beautiful” daughter died after living with a rare genetic disorder have told of their ...

1don MSN

Here's the truth about hoarding disorder – and how to help someone

Hoarding is a mental health disorder in which someone has an ongoing compulsion to hold onto their belongings.

EL PAÍS (English) on MSN1d

A genetic patch corrects a rare syndrome in human brain organoid grafted into a rat

The team led by Sergiu Pasca, from Stanford University, wants to test this promising strategy in children with Timothy ...

1d

Marlborough TikTok star, 11, with rare health disorder has earned millions of fans

Vitoria is a TikTok star at age 11, with 1.2 million followers and counting. Her handle, @grwms.by.vitoria, gives fans a ...

8 of family with rare genetic disorder cast votes from home

The eldest is 35 year sold and the youngest is 22 years old. “The current generation of the family is suffering from a ...

Dozens of genes are linked to post-traumatic stress disorder

Findings underscore that genetic factors contribute to development of the condition after a traumatic incident.

University of California19h

Breakthrough study on post-traumatic stress disorder

A UC San Diego-led collaboration of researchers, institutions and databases makes advances on the understanding of the ...

News Medical on MSN3h

Are parental psychiatric disorders related to the risk of autism spectrum disorder in the offspring?

The potential association between psychiatric disorders in parents and the risk of the offspring developing autism spectrum ...

1don MSN

Researchers uncover SNUPN gene responsible for a new muscular disorder

A study, published in Nature Communications, sheds light on a newly identified subtype of muscular dystrophy, revealing an ...

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