The Speak Foundation launched the LGMD Centers of Excellence, a network of clinics dedicated to improving care for people ...

Wheelchairs tend to be equated with disability, but columnist Patrick Moeschen sees them as tools that increase function and ...

Upsher-Smith launched Kymbee support websites offering guidance on treatment, access, and care for DMD patients, caregivers, ...

Columnist Betty Vertin affirms that being diagnosed with a rare disease like Duchenne MD doesn't diminish the value of her sons’ lives.

An industry collaborative was formed with the goal of improving the design of clinical trials testing new treatments for FSHD ...

Muscular dystrophy refers to a group of genetic diseases that cause progressive muscle weakness and loss. There are more than 30 types of muscular dystrophy, all with different causes and symptoms.

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

Betty Vertin is a mother and writer living in rural Hastings, Nebraska, with her husband and seven children. Betty is a caregiver to three sons, Max, Rowen, and Charlie. Her oldest was diagnosed with ...

While Duchenne muscular dystrophy (DMD) is one of the most common types of this group of muscle-wasting disorders, affecting about 1 in 3,500 male births, each patient’s journey with this form of ...

Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...

The U.S. Food and Drug Administration (FDA) has granted rare pediatric disease designation to SAT-3247, an oral treatment candidate for Duchenne muscular dystrophy (DMD) that ultimately aims to slow ...

Living with Duchenne muscular dystrophy (DMD) has affected my ability to do many things I used to love, such as brushing my teeth, dressing, sketching cartoons, eating snacks, handwriting assignments ...