Dosing has begun in a Phase 2 clinical trial testing the experimental oral therapy SAT-3247 in boys with Duchenne muscular ...
Columnist Shalom Lim has discovered that a personal sense of belonging is built through simple presence. Art can help foster ...
Lasting gains in swallowing ability have been reported for four people with oculopharyngeal muscular dystrophy given gene therapy in a trial.
Guest writer Matthew Busch says that, despite the setbacks and surgeries he's endured, he's now thriving in life with Duchenne MD.
A Phase 3 clinical trial testing SGT-003, a gene therapy candidate for Duchenne muscular dystrophy (DMD), will start dosing ...
A clinical trial testing Duchenne gene-editing therapy candidate PBGENE-DMD will soon launch in the U.S., having won ...
An honest answer about her sons would mean talking about all the things Duchenne MD has taken from them, writes columnist.
When faced with a bad moment or adverse event, columnist Patrick Moeschen says it helps to remember the rule of 10.
Dangerous snow and ice, along with FSHD symptoms, made it impossible for columnist Robin Stemple to leave his home for two weeks.
Aging with muscular dystrophy (MD) can involve gradual changes in strength, mobility, and daily functioning. Understanding MD progression can help you and your family anticipate these changes and plan ...
Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...