Columnist Shalom Lim enjoys "Les Misérables" in Singapore, and finds in the story of Jean Valjean the arc of his own life ...
Corticosteroid-related growth stunting in Duchenne muscular dystrophy might be partly reversed by switching to the medication Agamree, data suggest.
Rob Stemple is a lifelong advocate for people with disabilities. He was diagnosed with FSHD in 1971 at age 14. Rob struggled with its’ affects for over 50 years. He lost his eyesight in a devastating ...
Columnist Betty Vertin has begun doing three things to give herself time to recover from the business of her life as a Duchenne caregiver.
Bridgebio Pharma asked the FDA to approve BBP-418, an oral therapy that could be the first treatment for LGMD2i.
Early trial data suggest RNA therapies SRP-1001 and SRP-1003 reach muscle and show biomarker activity in muscular dystrophy.
Shalom Lim is a University of Liverpool graduate, having completed an honors bachelor’s degree in criminology and security in July 2021. Born with Duchenne muscular dystrophy and diagnosed at 4 months ...
Though he's often tempted to stay at home, columnist Patrick Moeschen is taking steps to prevent and combat social isolation.
Columnist Robin Stemple's latest excursion was a trek across the city to discover where to buy a lift chair for his ...
Sarepta plans to ask the FDA for full approval of exon-skipping Duchenne muscular dystrophy treatments Amondys 45 and Vyondys 53.
Doctors can use several tests to diagnose muscular dystrophy (MD). A correct diagnosis gives patients an understanding of how their disease is likely to progress. It also helps doctors do a better job ...