A long-term study found that heart health is generally stable over time in women carrying mutations that can cause MD types ...

Adults with MD in the U.S. report widespread gaps in sexual and reproductive healthcare, according to surveys and interviews ...

Dyne Therapeutics expects to report top-line data in early 2027 from its Phase 1/2 ACHIEVE trial testing zeleciment basivarsen (z-basivarsen), an experimental treatment for myotonic dystrophy type 1 ...

Your clinical hub for comprehensive DMD management. Explore expert-reviewed resources focused on early diagnosis, optimizing multidisciplinary interventions, and navigating emerging genetic therapies ...

Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...

A human being since 1972, Patrick Moeschen recently retired after 28 years of teaching music at the middle school level in a public school setting. Diagnosed with Becker muscular dystrophy (MD) in ...

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

While Duchenne muscular dystrophy (DMD) is one of the most common types of this group of muscle-wasting disorders, affecting about 1 in 3,500 male births, each patient’s journey with this form of ...

Going to school for the first time is an important moment in a child’s life. The educational journey for a child with Duchenne muscular dystrophy (DMD) can be exciting but also challenging. To smooth ...

Living with muscular dystrophy can be challenging, and there are considerations that must be taken into account on a day-to-basis and in certain situations to help patients manage the disease. Many ...

Symptoms typically first appear when patients reach middle age (around 40 to 60 years old). The initial symptoms are droopy eyelids and difficulty swallowing caused by the weakening of muscles around ...

People with Duchenne muscular dystrophy (DMD) require some level of caregiving throughout their whole lives, particularly as the disease progresses and patients become less mobile and more reliant on ...