Columnist Shalom Lim is grateful for the opportunity to use his lived experience to do good work on behalf of people with DMD ...

RGX-202 met the main goal of a Phase 3 DMD trial, and Regenxbio plans to seek accelerated approval for the gene therapy.

Seeing two sons with DMD lose the ability to walk isn't making the third son's disease progression any easier, says columnist Betty Vertin.

His daughter's graduation was a special day for columnist Robin Stemple and his family. But accessibility issues rained on ...

September 2026 Thu 17 Sam Osborn Memorial Golf Tournament September 17 - September 18 Tiburon Golf Club & Banquet Facility 10302 SOUTH 168TH STREET, OMAHA, NE, United States Join us for the annual Sam ...

MDA Engage – Chicago September 25 @ 7:00 PM - September 26 @ 4:45 PM Westin Chicago Lombard 70 Yorktown Shopping Center, Lombard, IL, United States Events Today Next Events Subscribe to calendar ...

July 2026 Sat 18 MDA Engage – Hershey, PA July 18 @ 8:30 AM - 5:00 PM Hershey Lodge - Confection Hall 325 University Drive, Hershey, PA, United States Join us for an energizing in person gathering ...

My dear friend Colin Rensch had a saying: “If you think you can, then of course you can.” I met Colin because I live with limb-girdle muscular dystrophy, and he lived with Duchenne muscular dystrophy.

Bridgebio is funding the MDA with $100,000 to advance projects aimed at improving multidisciplinary care for people with LGMD ...

Epicrispr Biotechnologies is partnering with Forge Biologics to support the development of EPI-321, an one-time epigentic ...

Duchenne Parent Project Spain is investing €247,000 in a project to create a new laboratory model to study heart health in ...

Columnist Betty Vertin shares a conversation with her daughter Lexi about finding out she was not a DMD gene carrier.