Columnist Robin Stemple wasn't thrilled with the idea of respite care, but it solves scheduling challenges he has with family ...

Ongoing steroid treatment was linked to slower lung-function decline and later breathing support in older teens and adults ...

The FDA is considering whether to conditionally approve a new treatment for DMD patients with mutations amenable to exon 51 ...

Columnist Betty Vertin shares big news about a bigger house her family is buying that will better accommodate her sons with Duchenne MD.

The MDA Engage seminar in Hershey, Pennsylvania, brought together neuromuscular families and specialists for education and ...

Able,” a short film starring my girlfriend, Amanda, and me, was selected for inclusion in AN/OTHER Film Festival in Fremantle ...

The Muscular Dystrophy Association (MDA) brought its Engage Community Seminar to Hershey, Pennsylvania, on July 18, uniting individuals with neuromuscular diseases, caregivers, and medical experts for ...

Commendamide, a metabolite produced by beneficial gut bacteria that are depleted in people with DMD, protects muscle cells ...

The U.S. Food and Drug Administration (FDA) has approved an update to the prescribing information for Duchenne muscular dystrophy (DMD) gene therapy Elevidys (delandistrogene moxeparvovec-rokl), ...

Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...

Muscular dystrophy (MD) refers to a group of inherited muscle disorders caused by mutations in genes that generate proteins that play an essential role in muscle structure and function. The disease ...