An industry collaborative was formed with the goal of improving the design of clinical trials testing new treatments for FSHD ...

Corticosteroid-related growth stunting in Duchenne muscular dystrophy might be partly reversed by switching to the medication Agamree, data suggest.

Columnist Betty Vertin affirms that being diagnosed with a rare disease like Duchenne MD doesn't diminish the value of her sons’ lives.

The FDA has given Mesoblast the go-ahead to launch a clinical trial testing its cell therapy remestemcel-L-rknd in children ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google Last Saturday, I attended “Les Misérables: The Arena Spectacular” ...

A human being since 1972, Patrick Moeschen recently retired after 28 years of teaching music at the middle school level in a public school setting. Diagnosed with Becker muscular dystrophy (MD) in ...

Columnist Betty Vertin has begun doing three things to give herself time to recover from the business of her life as a Duchenne caregiver.

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google As I grow older with limb-girdle muscular dystrophy, one of my ...

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

While Duchenne muscular dystrophy (DMD) is one of the most common types of this group of muscle-wasting disorders, affecting about 1 in 3,500 male births, each patient’s journey with this form of ...