Columnist Shalom Lim is using his lived experience with Duchenne muscular dystrophy to consult with organizations about ...
Capricor has reapplied for FDA approval of deramiocel, its therapy for DMD-related heart disease, and expects a decision by August 22.
Dyne Therapeutics' Z-basivarsen led to gains in motor function and cognition for myotonic dystrophy type 1, and is entering a ...
New presentations at MDA 2026 expand the understanding of how Duvyzat may help people with Duchenne muscular dystrophy.
Columnist Robin Stemple knows that his physical challenges aren't his fault, but that doesn't make it any easier to avoid ...
MDA 2026 keynote speaker John Crowley discussed with MD News Today the progress made in neuromuscular disease and the future ...
PGN-EDODM1, an experimental DM1 therapy from Pepgen, showed biomarker activity and splicing correction in an early clinical ...
The investigational gene therapy SGT-003 is showing early signs of safety and efficacy for Duchenne muscular dystrophy in a ...
A human being since 1972, Patrick Moeschen recently retired after 28 years of teaching music at the middle school level in a public school setting. Diagnosed with Becker muscular dystrophy (MD) in ...