The FDA asked Sarepta to pause all U.S. shipments of the DMD gene therapy Elevidys, and the company has agreed after initially refusing.

Columnist Patrick Moeschen emphasizes the importance of making advance directives and shares some tips for how to get started ...

While looking at a hotel mirror, columnist Betty Vertin reflects on the past 15 years of raising three sons with DMD.

The first patient has been dosed in a clinical trial testing Sardocor's one-time gene therapy for cardiomyopathy associated ...

Dealing with pain has become increasingly challenging for columnist Robin Stemple, who struggles to find relief from the hurt ...

Capricor plans to resubmit its application for the approval of deramiocel for DMD after the FDA declined to accept the ...

Capricor plans to resubmit its application for the approval of deramiocel for DMD after the FDA declined to accept the original proposal.

Columnist Betty Vertin embraces July's slower pace, a much-needed respite from caregiving demands for her family of nine.

A research team collected pain and prescription data from the medical records of 1,282 people with different types of ...

Columnist Shalom Lim is energized by a recent program for youth leaders in Singapore that matched them with people from the ...