The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, such as the liver, lungs, and spleen. Nevertheless, Ali and Townsend note ...

Born in Mumbai, Reshma moved to the United States at the age of 11. She earned her medical degree from Boston University and ...

Agios Pharmaceuticals gears up for a pivotal 2025 with key PYRUKYND milestones, including FDA decisions for thalassemia.

Some Boston public school students are spending their summer vacations learning and working at a global biotech company.

A cure for genetic heart conditions could reach trials in only 5 years, and it “rewrites” DNA. Experts explain the potential ...

Q2 2025 Earnings Conference Call July 31, 2025 8:30 AM ETCompany ParticipantsBrian Foard - Executive VP & Head of ...