Haematological cancers are a recognised potential side effect with Skysona and were already mentioned in a boxed warning on the gene therapy's approved labelling. The new label restricts use of the ...

At 22, Daniel Cressy is making history as Louisiana’s first sickle cell gene therapy patient. The treatment could be a cure ...

Detailed price information for Agios Pharmaceuticals (AGIO-Q) from The Globe and Mail including charting and trades.

Net loss (GAAP) widened to $2.6 million, driven by increased expenses from the GPCR Therapeutics USA Inc. acquisition. Management issued a going concern warning, citing $7.9 million in cash and cash ...

For the most part, the benefits to stroke patients from physical therapy plateau after about six months. Years after her ...

Below is a brief description of sickle cell disease and the populations most affected by it.SCD is a genetic blood disorder that affects the structure and function of red blood cells. In individuals ...

Overview: Quality Chemicals supplies HIV medicines to 14 countries in the region, with 17 million treatments sold last year, ...

After telegraphing an investigation in November, the FDA has moved to restrict the use of bluebird bio’s gene therapy Skysona ...

What Happened: SACHS's recent move, as outlined in a Form 4 filing with the U.S. Securities and Exchange Commission on Thursday, involves purchasing 5,000 shares of Vertex Pharmaceuticals. The total ...

NEW YORK, NY-Reshma Kewalramani, the Mumbai-born CEO of Vertex Pharmaceuticals, has been named one of the 100 Most Powerful ...

He recently had the first of two six-hour procedures at Manning Family Children's Hospital to collect his stem cells in order to edit them.

The FDA's approval of the first CRISPR-Cas9–based gene therapy marked a major milestone in biomedicine, validating genome ...