The firm sees the astonishingly high cost of "cellular, gene and RNA therapies" — high-tech treatments for conditions like ...

In head-to-head clinical trials, ALYFTREK was non-inferior on ppFEV1 and superior in reducing sweat chloride compared to ...

Acute chest syndrome associated with sickle cell is driven by the abnormal activation of the complement cascade, per a study.

Insiders have become bearish. In fact, according to MarketWatch, “Corporate insiders have taken a sharply pessimistic turn – ...

Vertex Pharmaceuticals is all set to release its fiscal second-quarter earnings next month, and analysts project a robust ...

PRNewswire/ - Medunik USA, a specialty pharmaceutical company dedicated to providing rare disease patients with access to ...

Sickle cell disease treatment progress has improved over the years, but recent federal cuts threaten the health of those who suffer from the blood ailment.

Sofia, 11, wouldn't be enjoying the simple pleasures of swimming, riding a bike and spending time with friends today had it ...

In a country where 90 per cent of children with sickle cell disease once died before their fifth birthday, Betty, 64, and ...

NRI PULSE STAFF REPORT The 2025 edition of TIME100 Most Influential Companies honors leaders and innovators who are ...

With promising new obesity treatments in the pipeline, 24/7 Wall St. projects huge upside for Novo Nordisk stock through 2030 ...

The Centers for Medicare & Medicaid Services (CMS) has unveiled a groundbreaking initiative aimed at expanding access to ...